HIGHLIGHTS
- who: Francesca Magri and colleagues from the Neurology Unit, IRCCS Fondazione Ca` Granda Ospedale Maggiore Policlinico, Milan, Italy Dino Ferrari Center, Department of Pathophysiology and Transplantation, University of Milan have published the Article: Antisense Morpholino-Based In Vitro Correction of a Pseudoexon-Generating Variant in the SGCB Gene, in the Journal: (JOURNAL)
- what: The authors report a novel LGMDR4 patient presenting as almost asymptomatic at 12 years of age and with repeated findings of high creatine-kinase levels. The establishment of patient-specific induced pluripotent stem_cells provided the work bench to test a morpholino oligomer . . .
If you want to have access to all the content you need to log in!
Thanks :)
If you don't have an account, you can create one here.