HIGHLIGHTS
- who: Laura Antonaci from the Centro Clinico Nemo, Fondazione Policlinico Universitario Agostino Gemelli IRCCS, Rome, Italy have published the research: New therapies for spinal muscular atrophy: where we stand and what is next, in the Journal: (JOURNAL)
- what: The aim of this paper is to provide the current therapeutic scenario including new perspectives and to report the challenges related to new phenotypes a few years after the therapies have become available. The other approaches aiming at increasing SMN protein use a different mechanism, targeting not the SMN1 gene but the homologous gene SMN2. Following suggestions . . .
If you want to have access to all the content you need to log in!
Thanks :)
If you don't have an account, you can create one here.