Fantastic aav gene therapy vectors and how to find them—random diversification, rational design and machine learning

HIGHLIGHTS

SUMMARY

    While these promoters tend to be leaky, they can minimize unwanted vector expression in off-targets and thereby increase in_vivo vector safety, especially when used in combination with capsids with a broad cell specificity. Pioneering work by Girod et_al identified these insertion sites by aligning the AAV2 capsid amino_acid sequence to the ones from canine parvovirus, for which the X-ray_crystal_structure was already available. A standard directed evolution approach for AAV capsid diversification is the insertion of random peptides into the previously identified capsid positions, followed by the use of in_vitro or in_vivo selection . . .

     

    Logo ScioWire Beta black

    If you want to have access to all the content you need to log in!

    Thanks :)

    If you don't have an account, you can create one here.

     

Scroll to Top

Add A Knowledge Base Question !

+ = Verify Human or Spambot ?